UNI
Wat is de waarde van uniQure?
Since last November, we’ve been waiting for more data from uniQure about the ongoing trial of AMT-130, expected in June. This release involves two years of data from the first, low-dose cohort of ten,...
22 jun 2023 12:18
UNI
Wat is de waarde van uniQure?
quote:DeZwarteRidder schreef op 21 juni 2023 16:57:[...]Uniqure zal uiteindelijk waardeloos eindigen.Hé Kraai, oeist?...
21 jun 2023 19:15
UNI
Wat is de waarde van uniQure?
Gene therapy can transform life for people with hemophilia. www.bostonglobe.com/2023/01/29/busine...The fir...
8 feb 2023 18:21
UNI
Wat is de waarde van uniQure?
Steven Pipe: If you get gene therapy treatment and are liberated from needing to remain on prophylaxis, thats an immediate cost savings every month, every year, and hopefully for decades afterwar...
1 dec 2022 12:09
UNI
Wat is de waarde van uniQure?
USA:In conclusion, based on detailed simulation inputs and assumptions, gene therapy was more cost-effective than on-demand treatment and prophylaxis for patients with severe #hemophiliaB The cost...
23 nov 2022 15:11
UNI
Wat is de waarde van uniQure?
quote:flosz schreef op 23 november 2022 09:03:Heb er zin in Prof. maar dinsdag eerst de wedstrijd.Zie door de benen de bal niet meer, zo ongeveer....
23 nov 2022 10:15
UNI
Wat is de waarde van uniQure?
Heb er zin in Prof. maar vrijdag eerst de wedstrijd.Hoi Voda, m’n bloemenman: mooi was die tijd....
23 nov 2022 09:03
UNI
Wat is de waarde van uniQure?
Allemaal gefeliciteerd !...
23 nov 2022 08:04
UNI
Hemofilie B; nog steeds on track?
At FDA meeting, gene therapy experts wrestle with fields blindspots www.biopharmadive.com/news/fda-gene-t...
3 sep 2021 19:37
UNI
Hemofilie B; nog steeds on track?
What to expect at the FDAs two-day meeting on gene therapy safetywww.biopharmadive.com/news/fda-gene-t...Food and Drug Administration ...
1 sep 2021 21:23
UNI
Wat is de waarde van uniQure?
[quote alias=harvester id=13306876 date=202103222255][...]Ik neem even aan dat die studie een andere invalshoek had als die van Uniqure.Dan zal er meer aandacht komen voor de andere studies....
1 apr 2021 00:22
GAL
Draadje OT, bijzaken & geleuter in de marge!
[quote alias=voda id=13316027 date=202103251415]Nederlandse start-up haalt 40 miljoen op voor corona-neusspraysGepubliceerd op 25 maart 2021 13:00 | Views: 1.761AMSTERDAM (ANP) - De Nederlan...
1 apr 2021 00:12
UNI
Hemofilie B; nog steeds on track?
twitter.com/mauriceontw/status/135439...
27 jan 2021 12:40
UNI
Huntington’s Disease
Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology res.mdpi.com/...
27 jan 2021 12:38
UNI
Hemofilie B; nog steeds on track?
Ter aanvulling.....( tweet Prof. Makris).Table adapted from Srivasta A, et al. Hemophilia. 2020;26:1-158WFH Guidelines for the Management of Hemophilia, 3rd edition.P.21. onlinelibrary...
9 dec 2020 15:29
UNI
Hemofilie B; nog steeds on track?
Gene therapies for the rare blood clotting disorder hemophilia B have taken a step closer to the market as Dutch developer $QURE became the first to release interim phase III results last week. https:...
9 dec 2020 11:37
UNI
Hemofilie B; nog steeds on track?
Art. 29 juni, 2020. Freeline.Dangerously high FIX levels reported in #hemophiliaB gene therapy. A patient reported his FIX levels had risen to over 500% of normal after receiving AAV-S3 (FLT-180...
9 dec 2020 11:31
UNI
Hemofilie B; nog steeds on track?
$QURE #ASH20 transcript Presentation S. Pipe assets.onlineeventapp.com/ash/annual2...
8 dec 2020 23:40
UNI
Hemofilie B; nog steeds on track?
$QURE #ASH2020 A Single Administration of AAV5-hFIX in Newborn, Juvenile and Adult Mice Leads to Stable hFIX Expression up to 18 Months after Dosing twitter.com/floszcrxl/status/13240075...
4 nov 2020 16:25
UNI
Huntington’s Disease
Door Melvin Evers. Geen significante risico’s bij eerste toepassing van gentherapie bij huntingtonpatiëntenIn juni 2020 is de eerste gentherapie toegepast op een patiënt met de ziekte van Hu...
29 okt 2020 13:19
UNI
Huntington’s Disease
Ralf Reilmann: First Human #AAV GeneTherapy Clinical Trial in Adults with Early Manifest HD. AMT-130 $QURE #HuntingtonsDisease vimeo.com/458068349 (44:03) twitter.com/floszcrxl/statu...
6 okt 2020 18:15
UNI
Wat is de waarde van uniQure?
Thx. Prof., mooi!...
28 sep 2020 14:17
UNI
PubMed UniQure
Transduction patterns in the CNS following various routes of AAV-5-mediated gene delivery. www.nature.com/articles/s41434-020-01...
18 aug 2020 20:08
KOF
Coronavirus echt gevaar?
Single-shot Ad26 vaccine protects against SARS-CoV-2 in rhesus macaques www.nature.com/articles/s41586-020-26...Ad26 PER.C6 $JNJ ($CRXL )Janssenwww.prnewswire....
30 jul 2020 11:50
GAL
Draadje OT, bijzaken & geleuter in de marge!
Single-shot Ad26 vaccine protects against SARS-CoV-2 in rhesus macaques www.nature.com/articles/s41586-020-26...Ad26 PER.C6 $JNJ ($CRXL )Janssen www.prnewswire...
30 jul 2020 11:48
UNI
Draadje OT, bijzaken & geleuter in de marge!
Single-shot Ad26 vaccine protects against SARS-CoV-2 in rhesus macaques www.nature.com/articles/s41586-020-26...Ad26 PER.C6 $JNJ ($CRXL )Janssen www.prnewswire.com...
30 jul 2020 11:47
KOF
Coronavirus echt gevaar?
Hearing on Vaccine Research Development with Pharmaceutical CompaniesPharmaceutical officials testified on COVID-19 vaccine research and development.www.c-span.org/video/?473931-1/...
21 jul 2020 17:29
GAL
Draadje OT, bijzaken & geleuter in de marge!
Hearing on Vaccine Research Development with Pharmaceutical CompaniesPharmaceutical officials testified on COVID-19 vaccine research and development.www.c-span.org/video/?473931-1/...
21 jul 2020 17:23
UNI
Draadje OT, bijzaken & geleuter in de marge!
Hearing on Vaccine Research Development with Pharmaceutical CompaniesPharmaceutical officials testified on COVID-19 vaccine research and development.www.c-span.org/video/?473931-1/...
21 jul 2020 17:22
UNI
Wat is de waarde van uniQure?
[quote alias=harvester id=12571432 date=202007142330][...]Waarom denk je dat Pfizer die moeite neemt.Is Pfizer niet blij dat de recente deal niet met hen is gesloten?Vinden ze de patenten ...
15 jul 2020 15:57
UNI
Huntington’s Disease
AAV5-miHTT gene therapy for #HuntingtonsDisease :lowering both huntingtins www.tandfonline.com/doi/abs/10.1080/1...
15 jul 2020 15:37
GAL
Draadje OT, bijzaken & geleuter in de marge!
Yesssssssssssss:$JNJ Announces European Commission Approval for Janssen’s Preventive Ebola Vaccine www.janssen.com/johnson-johnson-annou...
1 jul 2020 17:59
UNI
Draadje OT, bijzaken & geleuter in de marge!
Yesssssss:$JNJ Announces European Commission Approval for Janssen’s Preventive Ebola Vaccine www.janssen.com/johnson-johnson-annou...
1 jul 2020 17:57
UNI
Draadje OT, bijzaken & geleuter in de marge!
Freeline Announces Additional Financing Plans..... which could include an initial public offering in the United States.www.freeline.life/investors-media/new...
1 jul 2020 12:52
UNI
Huntington’s Disease
Ohio State Conducts First Gene Therapy Clinical Trial For Huntingtons Diseasewexnermedical.osu.edu/mediaroom/press...
1 jul 2020 12:45
UNI
ontwikkelingen Parkinson / Parkinson's disease
GDNF and Parkinson’s Disease: Where Next? A Summary from a Recent Workshop content.iospress.com/articles/journal...AAV2-GDNF for Advanced #ParkinsonsDisease ...
1 jul 2020 12:40
UNI
Wat is de waarde van uniQure?
[quote alias=T. Montana id=12523085 date=202006242313]Inderdaad. Dus als je Hem B en A eruit plukt, wat houdt je dan over? Een zuivere CNS speler, of zie ik iets over het hoofd? Als dat zo is, verge...
25 jun 2020 00:59
UNI
Wat is de waarde van uniQure?
HemA: well served market, feedback regulatory bodies, competitive landscape, clinical feasibility, partner interest: interest did not materialize.Fix-Super9 X Streep erdoor miQURE #SCA3 - #SCA...
25 jun 2020 00:59
UNI
Wat is de waarde van uniQure?
$QURE ‘s Kapusta/Cantor @ GS 41st Annual Global Healthcare ConferenceWebcast:kvgo.com/GSHC/uniQure-june-2020...
10 jun 2020 15:56
UNI
PubMed UniQure
Cerebral organoids: a human model for AAV capsid selection and therapeutic transgene efficacy in the brain. www.cell.com/molecular-therapy-family...
5 jun 2020 11:47
UNI
Spark Therapeutics, Inc. (ONCE)
PF-06838435 (SPK-9001, $ONCE) Hemophilia BMean Activity 22.9 (9.89)Peak Activity29.1 (11.63)twitter.com/_b_i_o_t_e_c_h_/status/12...
19 mei 2020 23:47
UNI
AMT-180 Hemophilia A
Hemophilia A Gene Therapy, AMT-180, Continues to Show Activity, Safety in Animals ..................AMT-180 is a gene therapy being developed by uniQure to treat hemophilia A patients, includi...
15 mei 2020 18:10
GAL
Draadje OT, bijzaken & geleuter in de marge!
twitter.com/floszcrxl/status/12605134...Begin van dit jaar kreeg Jelle van Tilburg (34) uit Bergen op Zoom te horen dat hij een kwaadaardige hersentumor had. In het Erasmus MC...
13 mei 2020 12:45
UNI
Draadje OT, bijzaken & geleuter in de marge!
twitter.com/floszcrxl/status/12605134...Begin van dit jaar kreeg Jelle van Tilburg (34) uit Bergen op Zoom te horen dat hij een kwaadaardige hersentumor had. In het Erasmus MC...
13 mei 2020 12:44
KOF
In de race voor een Coronavirus Vaccin - wie wint?
Hoe Nederland de kennis voor een kansrijk coronavaccin uit handen gaf.Brus: “Als het aan ons had gelegen, was Nederland bij een pandemie verzekerd geweest van voldoende vaccins, maar de overheid had n...
12 mei 2020 23:35
UNI
Wat is de waarde van uniQure?
uniQure VP Eileen Sawyer spoke with @MAPSmedaffairs about uniQures patient-centric approach to #genetherapy product development to effectively engage patients throughout the process and, ultimate...
12 mei 2020 20:19
UNI
Wat is de waarde van uniQure?
Twitter-draadje met ASGCT abstracts:twitter.com/floszcrxl/status/12555303...www.asgct.org/global/documents/abstra...
29 apr 2020 18:46
UNI
Wat is de waarde van uniQure?
Significant Presence at Upcoming American Society of Gene and Cell Therapy (ASGCT) Virtual Annual Meeting tools.eurolandir.com/tools/Pressrelea...
28 apr 2020 23:09
UNI
Wat is de waarde van uniQure?
www.investors.com/news/technology/qur...
24 apr 2020 19:30
GAL
Draadje OT, bijzaken & geleuter in de marge!
New data on Gilead’s remdesivir, released by accident, show no benefit for coronavirus patients. Company still sees reason for hope www.statnews.com/2020/04/23/data-on-g...
23 apr 2020 20:33